Asset

Deflazacort

PTC Therapeutics Inc. Common Stock

Revenue

No revenue reported in loaded filings.

Clinical trials (8)

NCT IDPhaseStatusStartCompletionSponsor nameTitle
NCT02251600phase1completed2014-12-012015-10-01PTC TherapeuticsA Pharmacokinetic Study of Oral Deflazacort in Children and Adolescent Subjects With Duchenne Muscular Dystrophy
NCT02286609phase1completed2014-12-012015-02-01PTC TherapeuticsA Single Dose Evaluation of the Effects of Moderate Hepatic Impairment on Deflazacort Pharmacokinetics
NCT02286622phase1completed2014-12-012015-02-01PTC TherapeuticsA Single Dose Evaluation of the Effects of Renal Impairment on Deflazacort Pharmacokinetics
NCT03642145phase3withdrawn2018-10-312021-07-31PTC TherapeuticsA Study of Deflazacort (Emflaza®) in Participants With Duchenne Muscular Dystrophy (DMD)
NCT03783923phase3terminated2019-10-312021-01-01PTC TherapeuticsA Study of Deflazacort (Emflaza®) in Participants With Limb-Girdle Muscular Dystrophy 2I (LGMD2I)

FDA applications (2)

ApplicationTypeApplicant
NDA 208684NDAPTC THERAPEUTICS INC
NDA 208685NDAPTC THERAPEUTICS INC

Marketed products (5)

  • EMFLAZA
  • EMFLAZA
  • EMFLAZA
  • EMFLAZA
  • EMFLAZA