Clinical Trials - SLDB

NCT IDTitleStatusPhasesStart DateCompletion DatePrimary Completion Date
NCT07160634A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)NOT_YET_RECRUITINGPHASE32025-102034-012029-01
NCT07180355A Study of SGT-212 Gene Therapy in Friedreich's AtaxiaNOT_YET_RECRUITINGPHASE12025-10-012032-02-292028-03-21
NCT07148089A Study of SGT-501 Gene Therapy in Catecholaminergic Polymorphic Ventricular Tachycardia (CPVT)NOT_YET_RECRUITINGPHASE12025-10-012031-052027-06
NCT06138639A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)RECRUITINGPHASE1, PHASE22024-05-062031-05-062027-05-06
NCT03368742Microdystrophin Gene Transfer Study in Adolescents and Children With DMDACTIVE_NOT_RECRUITINGPHASE1, PHASE22017-12-062026-10-152026-10-15