Clinical Trials - RNA

NCT IDTitleStatusPhasesStart DateCompletion DatePrimary Completion Date
NCT07008469Global Open-Label Extension Study of Del-desiran for the Treatment of DM1ENROLLING_BY_INVITATIONPHASE32025-07-252030-102030-08
NCT07038200A Study to Evaluate Del-brax (Also Referred to as AOC 1020) in Participants With FSHDRECRUITINGPHASE32025-06-102028-072028-05
NCT06547216Phase 2 Open-label Extension Study of AOC 1020 in Participants with Facioscapulohumeral Muscular Dystrophy (FSHD)ENROLLING_BY_INVITATIONPHASE22024-07-252028-042028-04
NCT06411288Global Study of Del-desiran for the Treatment of DM1ACTIVE_NOT_RECRUITINGPHASE32024-05-302026-092026-03
NCT06244082Ph2 Open-label Study of AOC 1044 in Duchenne Muscular Dystrophy Participants With Mutations Amenable to Exon44 SkippingACTIVE_NOT_RECRUITINGPHASE22024-01-222027-07-312027-04-30
NCT05747924Phase 1/2 Study of AOC 1020 in Participants With Facioscapulohumeral Muscular Dystrophy (FSHD)ACTIVE_NOT_RECRUITINGPHASE1, PHASE22023-04-042027-042026-10
NCT05670730Study of AOC 1044 in Healthy Adult Volunteers and Participants With Duchenne Muscular Dystrophy (DMD) Mutations Amenable to Exon 44 SkippingCOMPLETEDPHASE1, PHASE22022-11-092024-11-252024-11-25
NCT05479981Extension of AOC 1001-CS1 (MARINA) Study in Adult Myotonic Dystrophy Type 1 (DM1) PatientsCOMPLETEDPHASE22022-08-042025-09-102025-09-05
NCT05027269Study of AOC 1001 in Adult Myotonic Dystrophy Type 1 (DM1) PatientsCOMPLETEDPHASE1, PHASE22021-10-282023-02-142023-02-14