Clinical Trials - RCKT

NCT IDTitleStatusPhasesStart DateCompletion DatePrimary Completion Date
NCT07137338A Phase 1 AAV Gene Therapy Trial Evaluating Safety and Preliminary Efficacy of RP-A701 in Subjects With BAG3 Dilated CardiomyopathyNOT_YET_RECRUITINGPHASE12026-062029-062029-06
NCT06422351Clinical Trial to Evaluate the Efficacy of Gene Therapy for Pyruvate Kinase DeficiencyNOT_YET_RECRUITINGPHASE22024-082029-012026-11
NCT06092034A Gene Therapy Study of RP-A501 in Male Patients With Danon DiseaseRECRUITINGPHASE22023-09-052032-042028-04
NCT05885412A Phase 1, Dose Escalation Trial of RP-A601 in Subjects With PKP2 Variant-Mediated Arrhythmogenic Cardiomyopathy (PKP2-ACM)RECRUITINGPHASE12023-08-292026-092025-09
NCT04525352A Trial to Evaluate Safety and Efficacy of RP-L401-0120 in Subjects With Infantile Malignant OsteopetrosisTERMINATEDPHASE12020-11-192021-05-212021-05-21
NCT04248439Gene Therapy for Fanconi Anemia, Complementation Group AACTIVE_NOT_RECRUITINGPHASE22020-07-152026-052026-05
NCT04105166Gene Therapy for Pyruvate Kinase Deficiency (PKD)COMPLETEDPHASE12020-07-062025-06-092025-06-09
NCT04069533Lentiviral-mediated Gene Therapy for Pediatric Patients With Fanconi Anemia Subtype AACTIVE_NOT_RECRUITINGPHASE22019-11-282025-022025-02
NCT03812263A Clinical Trial to Evaluate the Safety and Efficacy of RP-L201 in Subjects With Leukocyte Adhesion Deficiency-ICOMPLETEDPHASE1, PHASE22019-08-302023-09-122023-09-12
NCT03882437Gene Therapy for Male Patients With Danon Disease (DD) Using RP-A501; AAV9.LAMP2BUNKNOWNPHASE12019-04-172025-03-242025-03-24
NCT03825783A Gene Therapy Trial to Evaluate the Safety and Efficacy of RP-L201 in Subjects With Leukocyte Adhesion Deficiency-IWITHDRAWNPHASE12019-04-152021-102021-10
NCT03814408A Clinical Trial to Evaluate the Safety of RP-L102 in Pediatric Subjects With Fanconi Anemia Subtype AUNKNOWNPHASE12019-01-112022-032020-12