| NCT06109181 | Gene Therapy for ACM Due to a PKP2 Pathogenic Variant | RECRUITING | PHASE1, PHASE2 | 2024-02-29 | 2027-02 | 2026-02 |
| NCT05400330 | Long-Term Follow-up of Gene Therapy for APOE4 Homozygote Alzheimer's Disease | ACTIVE_NOT_RECRUITING | PHASE1 | 2023-05-08 | 2028-11 | 2028-11 |
| NCT05445323 | Gene Therapy for Cardiomyopathy Associated With Friedreich's Ataxia | ACTIVE_NOT_RECRUITING | PHASE1, PHASE2 | 2022-08-24 | 2029-09 | 2029-09 |
| NCT03634007 | Gene Therapy for APOE4 Homozygote of Alzheimer's Disease | COMPLETED | PHASE1, PHASE2 | 2019-11-06 | 2024-11-07 | 2024-11-07 |