Clinical Trials - LRMR

NCT IDTitleStatusPhasesStart DateCompletion DatePrimary Completion Date
NCT06681766A Study to Assess Nomlabofusp in Adolescents and Children with Friedreich's AtaxiaRECRUITINGPHASE12024-12-062025-082025-08
NCT06447025An Open Label Extension Study of CTI-1601 in Subjects With Friedreich's AtaxiaENROLLING_BY_INVITATIONPHASE22024-01-252027-012027-01
NCT05579691A Double-Blind, Placebo-Controlled, Dose Exploration Study of CTI-1601 in Adult Subjects With Friedreich's AtaxiaCOMPLETEDPHASE22022-09-212023-12-042023-12-04
NCT04519567Multiple Ascending Dose Study of CTI-1601 Versus Placebo in Subjects With Friedreich's AtaxiaCOMPLETEDPHASE12020-07-312021-03-162021-03-16
NCT04176991Single Ascending Dose Study of CTI-1601 Versus Placebo in Subjects With Friedreich's AtaxiaCOMPLETEDPHASE12019-12-112020-10-312020-10-31