{"nct_id":"NCT01230801","title":"Safety/Tolerability/Pharmacokinetic (PK)/Pharmacodynamics (PD) Study of BMN701 in Patients With Late-Onset Pompe Disease","status":"COMPLETED","status_verified_date":"2018-05","start_date":"2011-01-17","start_date_type":"ACTUAL","primary_completion_date":"2013-03-06","primary_completion_date_type":"ACTUAL","completion_date":"2013-03-06","completion_date_type":"ACTUAL","phases":["PHASE1","PHASE2"],"tickers":["BMRN"]}